CAR T Wins in Myeloma, Gene Therapy for WAS, and Human Neurons in Mice

Today we cover a high response CAR T-cell trial for relapsed multiple myeloma, a gene therapy success story for Wiskott-Aldrich syndrome, and new German consensus guidance on treating transthyretin amyloid heart disease. We also look at a chemotherapy-free approach for EGFR-mutant lung cancer, a disappointing ALS trial, and a wild new platform for growing human brain tissue inside mice.